Normal Function
The CDC73 gene (formerly known as HRPT2) provides instructions for making a protein called parafibromin. This protein is found primarily in the nucleus of cells and is likely involved in regulating gene transcription, which is the first step in protein production. Parafibromin functions as a tumor suppressor, which means it keeps cells from growing and dividing (proliferating) too rapidly or in an uncontrolled way. When parafibromin is found outside the nucleus, it appears to be involved in the organization of the cell's structural framework (the cytoskeleton).
Health Conditions Related to Genetic Changes
Familial isolated hyperparathyroidism
Variants (also called mutations) in the CDC73 gene have been found in some families with familial isolated hyperparathyroidism, a condition characterized by overactivity of the parathyroid glands (primary hyperparathyroidism). These glands release a hormone that helps control the normal balance of calcium in the blood. Primary hyperparathyroidism disrupts this balance, which can lead to high levels of calcium in the blood (hypercalcemia), kidney stones, thinning of the bones (osteoporosis), nausea, vomiting, high blood pressure (hypertension), weakness, and fatigue.
The CDC73 gene variants that cause familial isolated hyperparathyroidism reduce the activity of the parafibromin protein. Reduced parafibromin activity can increase cell proliferation, leading to the formation of tumors in the parathyroid glands. Parathyroid tumors in people with familial isolated hyperparathyroidism are usually noncancerous (benign). The tumors cause the glands to be overactive, resulting in primary hyperparathyroidism.
The variants associated with familial isolated hyperparathyroidism are thought to have a less severe effect on protein function than those that cause hyperparathyroidism-jaw tumor syndrome (described below). Occasionally, individuals with familial isolated hyperparathyroidism develop features of hyperparathyroidism-jaw tumor syndrome, although some never do. Familial isolated hyperparathyroidism caused by CDC73 gene variants may be an early or mild form of hyperparathyroidism-jaw tumor syndrome.
More About This Health ConditionHyperparathyroidism-jaw tumor syndrome
Variants in the CDC73 gene have been found to cause hyperparathyroidism-jaw tumor syndrome, which is a condition characterized by parathyroid tumors that cause hyperparathyroidism. People with this condition also have an increased risk of other benign tumors in the jaw, kidneys, and uterus. Hyperparathyroidism disrupts the normal balance of calcium in the blood, which can lead to kidney stones, osteoporosis, nausea, vomiting, hypertension, weakness, and fatigue in people with hyperparathyroidism-jaw tumor syndrome.
Most of the CDC73 gene variants that cause this condition can cause the cell to produce a version of the parafibromin protein that is abnormally short and does not function properly. Without functional parafibromin, cell proliferation is not properly regulated. Uncontrolled cell division can lead to the formation of tumors in people with hyperparathyroidism-jaw tumor syndrome. Parathyroid tumors, which can be benign or cancerous, interfere with the gland's normal function and lead to hyperparathyroidism in people with hyperparathyroidism-jaw tumor syndrome.
More About This Health ConditionParathyroid cancer
Variants in the CDC73 gene are found in up to 70 percent of people with parathyroid cancer. Of these individuals, approximately one-third inherit the variant from a parent, and the variant is present in all of the body's cells (germline mutation). In the remaining two-thirds of individuals, the CDC73 gene variant occurs in parathyroid cells during the person's lifetime (somatic mutation). However, not everyone who has a variant in the CDC73 gene will ultimately develop parathyroid cancer. Other genetic and nongenetic factors also contribute to a person's cancer risk.
In individuals with either a germline or somatic CDC73 gene variant, a second variant in the other copy of the CDC73 gene must occur for parathyroid cancer to develop. Parathyroid cells with two altered copies of the CDC73 gene produce no functional parafibromin. As a result, the cells grow and divide unchecked, which can lead to parathyroid cancer.
A significantly increased risk of parathyroid cancer is a feature of hyperparathyroidism-jaw tumor syndrome and familial isolated hyperparathyroidism (both described above). Parathyroid cancer occurs in 15 percent of individuals with hyperparathyroidism-jaw tumor syndrome and in 1 percent of individuals with familial isolated hyperparathyroidism. It is unclear why some people with a CDC73 gene variant will develop isolated parathyroid cancer while others will develop noncancerous tumors in the parathyroid glands and jaw or, hyperparathyroidism.
More About This Health ConditionOther Names for This Gene
- C1orf28
- CDC73_HUMAN
- cell division cycle protein 73 homolog
- HRPT2
- hyperparathyroidism 2 protein
- hyrax
- HYX
- parafibromin
Additional Information & Resources
Tests Listed in the Genetic Testing Registry
Scientific Articles on PubMed
Catalog of Genes and Diseases from OMIM
References
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